Intellia’s CRISPR therapy likely causes ‘permanent’ gene knockdown in ATTR amyloidosisnews2025-05-19T15:14:34+00:00May 19th, 2025|Endpoints News|
David Liu, Sam Sternberg unveil new way to insert big genes in human cellsnews2025-05-19T14:31:07+00:00May 19th, 2025|Endpoints News|
Apnimed posts first set of Phase 3 sleep apnea results, aims for approval filing in 2026news2025-05-19T10:00:51+00:00May 19th, 2025|Endpoints News|
Sarepta seeks to expand Duchenne gene therapy Elevidys use to toddlersnews2025-05-16T19:50:15+00:00May 16th, 2025|Endpoints News|
#ASGCT25: Lower conference attendance mirrors challenged cell and gene fieldnews2025-05-16T16:33:44+00:00May 16th, 2025|Endpoints News|
#ASGCT25: In three patients, Rocket’s second heart gene therapy shows promisenews2025-05-16T15:25:53+00:00May 16th, 2025|Endpoints News|
Kennedy adopts new chikungunya vaccine guidance, but other actions waitnews2025-05-16T02:05:29+00:00May 16th, 2025|Endpoints News|
Philadelphia doctors treat infant with first custom CRISPR therapy that fixes genetic mutationnews2025-05-15T17:00:12+00:00May 15th, 2025|Endpoints News|
Advocacy groups and experts call for decade-long ban on germline editingnews2025-05-14T10:00:09+00:00May 14th, 2025|Endpoints News|
Arcturus to prioritize mRNA therapeutics in bid to boost rare disease programsnews2025-05-13T15:07:41+00:00May 13th, 2025|Endpoints News|
